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Ngalaba Ọgwụgwọ
Ọgwụgwọ Ndị A Maara

Ngwunye Sodium nke Nusinersen: Olileanya maka Mgbu Ọkpụkpụ Spinal

Ngwunye Nusinersen Sodium bụ ọgwụgwọ mgbanwe maka Spinal Muscular Atrophy (SMA), ọrịa neuromuscular dị ụkọ nke na-akpata mfu akwara moto, na-ebute nnukwu atrophy na adịghị ike. Dịka ọgwụgwọ mbụ a kwadoro n'ụwa maka 5q SMA, ọ gbanweela nsonaazụ ndị ọrịa n'ụwa niile.

    Otu O Si Arụ Ọrụ

    Sodium Nusinersenbụ ọgwụgwọ antisense oligonucleotide (ASO) nke na-elekwasị anya na mkpụrụ ndụ ihe nketa SMN2.

      

    Site n'ịgbanwe usoro njikọta ya, ọ na-eme ka mmepụta nke ọrụ dịkwuo mma SMN proteindị mkpa maka ndụ na ọrụ nke akwara moto.

      

    A na-enye ọgwụ ahụ ozugbo n'ime mmiri cerebrospinal site na ịpịa lumbar, na-eme ka o ruo ebe ndị ahụ metụtara nke ọma.

    Uru Ọgwụ

    Ụdị SMA nke Mbụ:

    • Na-eme ka ọnụego ndụ afọ abụọ dịkwuo elu site na 50% nke akụkọ ihe mere eme ruo ihe karịrị 80%.
    • Na-eme ka ọrụ moto dịkwuo mma dịka ịnọdụ ala n'adabereghị onwe ya na njikwa isi.
    • Na-ebelata ịdabere na ventilator.

    SMA Ụdị nke Abụọ na nke Atọ:

    • Na-ebelata ọganihu ọrịa.
    • Na-ejigide ma ọ bụ na-eme ka mmegharị ụkwụ na ọrụ iku ume ka mma.
    • Ọgwụgwọ tupu mgbaàmà (dịka ọmụmaatụ, n'ime ụmụ amụrụ ọhụrụ) nwere ike ibute mmepe mmegharị ahụ fọrọ nke nta ka ọ bụrụ nke nkịtị.

    Mmetụta Ogologo Oge:

    • Data nleba anya afọ ise na-egosi mmezi ọrụ moto kwụsiri ike na-enweghị mbelata dị ukwuu.

    Nnweta zuru ụwa ọnụ:

    • Kemgbe FDA kwadoro ya na 2016, ihe karịrị ndị ọrịa 100,000 n'ofe mba 60+ eritela uru, na-ekpuchi ụdị SMA niile.

    Ihe akaebe sitere na Nnyocha

    Nnwale ahụike (dịka ọmụmaatụ, EMBRACE, ENDEAR, CHERISH) gụnyere Ndị ọrịa 274 gosipụta mmezi dị mkpa:

    • Nzaghachi dị mkpa nke moto: 51% ka mma karịa otu njikwa (p
    • Mmezi akara HINE-2: 26% ka mma karịa njikwa (p
      Ọmụmụ ihe ndị e mere n'oge ntorobịa na ndị okenye na-egosikwa na e nwere mmụba n'ọrụ mmegharị ahụ (dịka ọmụmaatụ, HFMSE, RULM) mgbe ọnwa iri abụọ na isii gachara.

    Ọnụ ego na BIOOCUS

    MUsoro Ọgwụgwọ Mbụ (Ọgwụ Mgbochi 4): Ngwugwu zuru oke nke $200,000, gụnyere:

    • Ọnụ ego ọgwụ: $50,000 kwa ọgwụ mgbochi.
    • Ụgwọ ịgba ọgwụ mgbochi, ngalaba, na ụgwọ nyocha.
    • Ọrụ mbufe ọdụ ụgbọ elu na ọrụ njem oyi.

    Ọgwụgwọ Mgbe Ọ BụsịrịNdị ọrịa nwere ike iji ọgwụ nke anọ laa n'ụlọ n'ime igbe yinye oyi nke 2-8°C ma nweta nkwado maka ọgwụ mmezi kwa ọnwa anọ.

    MNtụnyere Ọnụ Ego Mba Nile

    Obodo/Mpaghara

    Ọnụ ego kwa ịgba ọgwụ (USD)

    Ngụkọta maka Ọnụọgụ Ibu anọ (USD)

    Ọnụ ego Afọ Mbụ (USD)

    Ihe ndetu

    BIOOCUS, Chaịna

    50,000

    200,000

    200,000 (mmalite)

    Gụnyere ọrụ zuru oke

    United States

    125,000

    500,000

    750,000 (ọgwụ mgbochi isii)

    Enweghị enyemaka ego

    Ọstrelia

    87,500 (Enweghị enyemaka ego)

    350,000

    525,000 (ọgwụ mgbochi isii)

    Enyere PBS aka

     

    Nchekwa ego: Ọnụahịa BIOOCUS na-enye mbelata ọnụ ahịa ruo 60% ma e jiri ya tụnyere ọnụego enweghị nkwado na US na Australia.

    Nlekọta zuru oke maka ndị ọrịa mba ụwa

    Anyị na-enye nkwado pụrụ iche maka ndị ọrịa mba ofesi na-achọ ọgwụgwọ na China, na-eme ka ahụmịhe ahụ dị mma ma dịkwa mma.

    Tupu Ọgwụgwọ

    • Ndụmọdụ Ahụike: Atụmatụ ọgwụgwọ ahaziri ahazi dabere na ndekọ ndị ọrịa.
    • Ndị otu ọkachamara: Nchọpụta ọtụtụ ngalaba maka izi ezi.
    • Lọjistik: Enyemaka Visa, nhazi ego, na nhazi ụgbọelu.

    N'oge Ọgwụgwọ

    • Ebe Obibi na Njem: A haziri ndokwa maka ọnụnọ na nnyefe ọdụ ụgbọ elu maka ụlọ nkwari akụ.
    • Nlekọta AhụikeỌgwụgwọ na China Nuklia Medical Health Management Center, nke nwere teknụzụ dị elu na ndị ọrụ nwere nkà.
    • Usoro Ọgwụ Ntụtụ: A na-enye ya n'ụbọchị nke mbụ, nke iri na anọ, na nke iri abụọ na asatọ, yana nlele awa isii mgbe a gbasịrị ya ọgwụ maka nchekwa.

    Mgbe Ọgwụgwọ Gasịrị

    • Ọnụọgụ a na-ewere n'ụlọ: A na-enye ọgwụ nke anọ n'ime igbe yinye oyi.
    • Nkwado Na-aga n'ihu: Enyemaka maka usoro mmezi kwa ọnwa anọ, gụnyere ịzụta na mbupu.

    Ọrụ Ndị Ọzọ

    • Nkwurịta okwu: Nhazi WhatsApp na WeChat maka kọntaktị dị mfe.
    • Nweta VIPỌrụ ahụike a na-enyocha ngwa ngwa site n'aka ndị otu raara onwe ha nye.
    • Mkpa Kwa Ụbọchị: Nkwado maka ebe obibi, njem, iri nri, ịzụ ahịa, na nsụgharị ọkachamara.

    Submit An Free Inquiry

    Our medical team will make an evaluation for you, based on the information you provided. This procedure is free of charge.

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