- Ọgwụgwọ
- Ihe akaebe
- Neuroblastoma
- Ọrịa siri ike
- Ihe akaebe
- TILS
- Ọgwụgwọ NK Cell
- Myasthenia Gravis (MG)
- Ọrịa kansa ọbara Lymphoblastic dị oke njọ (B-ALL)
- Ọrịa Lupus Erythematosus Sistemụ (SLE)
- Ọrịa kansa ọbara Lymphoblastic dị oke njọ (T-ALL)
- Ọrịa Lymphoma na-abụghị Hodgkin (NHL)
- Ọtụtụ Myeloma (MM)
- Lymphom B-cell buru ibu nke gbasaara agbasa
- Ọrịa kansa ọbara B-lymphocytic
- Myeloma
Ngwunye Sodium nke Nusinersen: Olileanya maka Mgbu Ọkpụkpụ Spinal
Otu O Si Arụ Ọrụ
Sodium Nusinersenbụ ọgwụgwọ antisense oligonucleotide (ASO) nke na-elekwasị anya na mkpụrụ ndụ ihe nketa SMN2.
Site n'ịgbanwe usoro njikọta ya, ọ na-eme ka mmepụta nke ọrụ dịkwuo mma SMN proteindị mkpa maka ndụ na ọrụ nke akwara moto.
A na-enye ọgwụ ahụ ozugbo n'ime mmiri cerebrospinal site na ịpịa lumbar, na-eme ka o ruo ebe ndị ahụ metụtara nke ọma.
Uru Ọgwụ
Ụdị SMA nke Mbụ:
- Na-eme ka ọnụego ndụ afọ abụọ dịkwuo elu site na 50% nke akụkọ ihe mere eme ruo ihe karịrị 80%.
- Na-eme ka ọrụ moto dịkwuo mma dịka ịnọdụ ala n'adabereghị onwe ya na njikwa isi.
- Na-ebelata ịdabere na ventilator.
SMA Ụdị nke Abụọ na nke Atọ:
- Na-ebelata ọganihu ọrịa.
- Na-ejigide ma ọ bụ na-eme ka mmegharị ụkwụ na ọrụ iku ume ka mma.
- Ọgwụgwọ tupu mgbaàmà (dịka ọmụmaatụ, n'ime ụmụ amụrụ ọhụrụ) nwere ike ibute mmepe mmegharị ahụ fọrọ nke nta ka ọ bụrụ nke nkịtị.
Mmetụta Ogologo Oge:
- Data nleba anya afọ ise na-egosi mmezi ọrụ moto kwụsiri ike na-enweghị mbelata dị ukwuu.
Nnweta zuru ụwa ọnụ:
- Kemgbe FDA kwadoro ya na 2016, ihe karịrị ndị ọrịa 100,000 n'ofe mba 60+ eritela uru, na-ekpuchi ụdị SMA niile.
Ihe akaebe sitere na Nnyocha
Nnwale ahụike (dịka ọmụmaatụ, EMBRACE, ENDEAR, CHERISH) gụnyere Ndị ọrịa 274 gosipụta mmezi dị mkpa:
- Nzaghachi dị mkpa nke moto: 51% ka mma karịa otu njikwa (p
- Mmezi akara HINE-2: 26% ka mma karịa njikwa (p
Ọmụmụ ihe ndị e mere n'oge ntorobịa na ndị okenye na-egosikwa na e nwere mmụba n'ọrụ mmegharị ahụ (dịka ọmụmaatụ, HFMSE, RULM) mgbe ọnwa iri abụọ na isii gachara.
Ọnụ ego na BIOOCUS
MUsoro Ọgwụgwọ Mbụ (Ọgwụ Mgbochi 4): Ngwugwu zuru oke nke $200,000, gụnyere:
- Ọnụ ego ọgwụ: $50,000 kwa ọgwụ mgbochi.
- Ụgwọ ịgba ọgwụ mgbochi, ngalaba, na ụgwọ nyocha.
- Ọrụ mbufe ọdụ ụgbọ elu na ọrụ njem oyi.
Ọgwụgwọ Mgbe Ọ BụsịrịNdị ọrịa nwere ike iji ọgwụ nke anọ laa n'ụlọ n'ime igbe yinye oyi nke 2-8°C ma nweta nkwado maka ọgwụ mmezi kwa ọnwa anọ.
MNtụnyere Ọnụ Ego Mba Nile
| Obodo/Mpaghara | Ọnụ ego kwa ịgba ọgwụ (USD) | Ngụkọta maka Ọnụọgụ Ibu anọ (USD) | Ọnụ ego Afọ Mbụ (USD) | Ihe ndetu |
| BIOOCUS, Chaịna | 50,000 | 200,000 | 200,000 (mmalite) | Gụnyere ọrụ zuru oke |
| United States | 125,000 | 500,000 | 750,000 (ọgwụ mgbochi isii) | Enweghị enyemaka ego |
| Ọstrelia | 87,500 (Enweghị enyemaka ego) | 350,000 | 525,000 (ọgwụ mgbochi isii) | Enyere PBS aka
|
Nchekwa ego: Ọnụahịa BIOOCUS na-enye mbelata ọnụ ahịa ruo 60% ma e jiri ya tụnyere ọnụego enweghị nkwado na US na Australia.
Nlekọta zuru oke maka ndị ọrịa mba ụwa
Anyị na-enye nkwado pụrụ iche maka ndị ọrịa mba ofesi na-achọ ọgwụgwọ na China, na-eme ka ahụmịhe ahụ dị mma ma dịkwa mma.
Tupu Ọgwụgwọ
- Ndụmọdụ Ahụike: Atụmatụ ọgwụgwọ ahaziri ahazi dabere na ndekọ ndị ọrịa.
- Ndị otu ọkachamara: Nchọpụta ọtụtụ ngalaba maka izi ezi.
- Lọjistik: Enyemaka Visa, nhazi ego, na nhazi ụgbọelu.
N'oge Ọgwụgwọ
- Ebe Obibi na Njem: A haziri ndokwa maka ọnụnọ na nnyefe ọdụ ụgbọ elu maka ụlọ nkwari akụ.
- Nlekọta AhụikeỌgwụgwọ na China Nuklia Medical Health Management Center, nke nwere teknụzụ dị elu na ndị ọrụ nwere nkà.
- Usoro Ọgwụ Ntụtụ: A na-enye ya n'ụbọchị nke mbụ, nke iri na anọ, na nke iri abụọ na asatọ, yana nlele awa isii mgbe a gbasịrị ya ọgwụ maka nchekwa.
Mgbe Ọgwụgwọ Gasịrị
- Ọnụọgụ a na-ewere n'ụlọ: A na-enye ọgwụ nke anọ n'ime igbe yinye oyi.
- Nkwado Na-aga n'ihu: Enyemaka maka usoro mmezi kwa ọnwa anọ, gụnyere ịzụta na mbupu.
Ọrụ Ndị Ọzọ
- Nkwurịta okwu: Nhazi WhatsApp na WeChat maka kọntaktị dị mfe.
- Nweta VIPỌrụ ahụike a na-enyocha ngwa ngwa site n'aka ndị otu raara onwe ha nye.
- Mkpa Kwa Ụbọchị: Nkwado maka ebe obibi, njem, iri nri, ịzụ ahịa, na nsụgharị ọkachamara.
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