- Mankhwala
- Umboni
- Neuroblastoma
- Chotupa Cholimba
- Umboni
- TILS
- Chithandizo cha Maselo a NK
- Myasthenia Gravis (MG)
- Khansa ya m'magazi ya Lymphoblastic (B-ALL)
- Systemic Lupus Erythematosus (SLE)
- Matenda a khansa ya m'magazi (T-ALL)
- Non Hodgkin Lymphoma (NHL)
- Matenda a Myeloma Yambiri (MM)
- Kufalitsa Lymphom Yaikulu ya B-cell
- B-lymphocytic Leukemia
- Myeloma
Jekeseni wa Nusinersen Sodium: Chiyembekezo cha Kufooka kwa Minofu ya Msana
Momwe Zimagwirira Ntchito
Nusinersen Sodiumndi mankhwala oletsa kumva a oligonucleotide (ASO) omwe amalimbana ndi majini a SMN2.
Mwa kusintha njira yake yolumikizira, imawonjezera kupanga kwa ntchito Puloteni ya SMN, chofunikira kwambiri kuti ma neuron azitha kugwira ntchito bwino komanso kuti apulumuke.
Mankhwalawa amaperekedwa mwachindunji mu cerebrospinal fluid kudzera mu lumbar puncture, kuonetsetsa kuti afika bwino m'malo okhudzidwawo.
Ubwino Wachipatala
Mtundu wa SMA Woyamba:
- Kuchulukitsa kuchuluka kwa moyo wa zaka ziwiri kuchokera pa 50% yakale kufika pa 80%.
- Zimathandizira magwiridwe antchito a thupi monga kukhala pawokha komanso kulamulira mutu.
- Amachepetsa kudalira ma ventilator.
SMA Type II ndi III:
- Amachepetsa kukula kwa matenda.
- Kumasunga kapena kukonza kuyenda kwa miyendo ndi kupuma.
- Chithandizo cha zizindikiro zisanachitike (monga mwa makanda obadwa kumene) chingayambitse kukula kwa minofu ya thupi ngati yachibadwa.
Zotsatira Za Nthawi Yaitali:
- Deta yotsatira ya zaka zisanu ikuwonetsa kusintha kwa magwiridwe antchito a minofu popanda kuchepa kwakukulu.
Kufikira Padziko Lonse:
- Kuyambira pomwe FDA idavomereza mu 2016, odwala opitilira 100,000 m'maiko opitilira 60 apindula, kuphatikiza mitundu yonse ya SMA.
Umboni Wochokera ku Kafukufuku
Mayeso azachipatala (monga, EMBRACE, ENDEAR, CHERISH) okhudza Odwala 274 onetsani kusintha kwakukulu:
- Yankho la mfundo zazikulu za injini: 51% bwino kuposa magulu olamulira (p
- Kukweza kwa HINE-2: 26% bwino kuposa zowongolera (p
Kafukufuku mwa achinyamata ndi akuluakulu akuwonetsanso kuchuluka kwa magwiridwe antchito a minofu (monga HFMSE, RULM) patatha miyezi 26.
Mitengo ku BIOOCUS
IneKuyamba kwa Chithandizo (Majakisoni 4): Phukusi lonse la $200,000, kuphatikizapo:
- Mtengo wa mankhwala: $50,000 pa jakisoni.
- Ndalama zolipirira jakisoni, chipinda chogona, ndi zolipirira mayeso.
- Kusamutsa anthu ku eyapoti ndi ntchito zoyendera anthu oyenda pansi pa madzi ozizira.
Pambuyo pa ChithandizoOdwala akhoza kutenga mlingo wachinayi kunyumba m'bokosi lozizira la 2-8°C ndikulandira chithandizo cha mankhwala osamalira miyezi inayi iliyonse.
IneKuyerekeza Mtengo Wapadziko Lonse
| Dziko/Chigawo | Mtengo pa jakisoni (USD) | Chiwerengero cha Mlingo 4 Wokweza (USD) | Mtengo wa Chaka Choyamba (USD) | Zolemba |
| BIOOCUS, China | 50,000 | 200,000 | 200,000 (yoyamba) | Kuphatikizapo ntchito zonse |
| United States | 125,000 | 500,000 | 750,000 (jakisoni 6) | Palibe thandizo la ndalama |
| Australia | 87,500 (Palibe thandizo la ndalama) | 350,000 | 525,000 (jakisoni 6) | PBS Yothandizidwa ndi Ndalama
|
Ndalama zosungidwaMitengo ya BIOOCUS ikupereka kuchepetsedwa kwa mtengo mpaka 60% poyerekeza ndi mitengo yosathandizidwa ku US ndi Australia.
Chisamaliro Chokwanira cha Odwala Padziko Lonse
Timapereka chithandizo chapadera kwa odwala ochokera kumayiko ena omwe akufuna chithandizo ku China, zomwe zimawatsimikizira kuti ali ndi chithandizo chosavuta komanso chomasuka.
Musanalandire Chithandizo
- Uphungu wa Zachipatala: Mapulani a chithandizo omwe amapangidwa ndi munthu payekha kutengera zolemba za wodwala.
- Gulu la Akatswiri: Kuzindikira matenda m'magawo osiyanasiyana kuti mudziwe molondola.
- Kayendetsedwe ka zinthuThandizo la Visa, kulinganiza ndalama zolipirira, ndi makonzedwe a ndege.
Pa Nthawi ya Chithandizo
- Malo Ogona ndi Maulendo: Malo okhala ku hotelo ndi kusamutsa anthu kupita ku eyapoti kwakonzedwa.
- Chisamaliro cha ZamankhwalaChithandizo ku China Nuclear Medical Health Management Center, chomwe chili ndi ukadaulo wapamwamba komanso antchito aluso.
- Ndondomeko Yopangira Jakisoni: Amaperekedwa pa tsiku 1, 14, ndi 28, ndi kuyang'aniridwa kwa maola 6 pambuyo pa jakisoni kuti atsimikizire chitetezo.
Pambuyo pa Chithandizo
- Mlingo Wotengera Kunyumba: Jakisoni wachinayi waperekedwa m'bokosi la unyolo wozizira.
- Thandizo LopitiliraThandizo pa mlingo wokonza miyezi inayi iliyonse, kuphatikizapo kugula ndi kutumiza.
Ntchito Zowonjezera
- Kulankhulana: WhatsApp ndi WeChat kukhazikitsa kuti zikhale zosavuta kulankhulana.
- Kupeza Anthu Otchuka: Utumiki wachipatala wofulumira kudzera m'magulu odzipereka.
- Zosowa za Tsiku ndi Tsiku: Chithandizo cha malo ogona, mayendedwe, chakudya, kugula zinthu, ndi kumasulira kwaukadaulo.
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