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FUCASO: Ko te Whakatairanga Tino-tangata BCMA CAR-T Therapy me te kaha me te haumaru kore e rite.

Ko te FUCASO he rongoa CAR-T hurihuri a BCMA-whakaaro na IASO BIO, e tuku ana i te whaihuatanga me te haumarutanga mo te myeloma maha kua hoki whakamuri, whakakeke ranei. Na te nui o nga reeti whakautu, te roa o te murunga, me te tohu haumaru pakari, ka whakarato a FUCASO i te tumanako hou mo nga turoro me te whakatakoto i tetahi paerewa hou mo te rongoa CAR-T.

    taipitopito hua

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    Ko te FUCASO, i whakawhanakehia e Nanjing IASO Biotechnology, he rongoa CAR-T hou i hangaia ki te whai i te antigen matuatanga pūtau-B (BCMA). Ko tenei rongoa e tu mai ana mo tana whaihua haumanu kore rite me tana tohu haumaru, e whakarato ana i te tumanako hou mo nga turoro me te mate mieloma maha (r/rMM) kua hoki mai. I whakaaetia e te National Medical Products Administration (NMPA) i te Pipiri 30, 2023, kua whakaatuhia e FUCASO te angitu nui i roto i nga tono haumanu.

    Nga Painga Matua o FUCASO

    Reiti Whakautu Nui: Kei te whakanui a FUCASO i te Reiti Whakautu Katoa (ORR) o 98.9% me te reeti Whakautu Katoa (CR) o 82.4%, tino teitei ake i etahi atu maimoatanga e waatea ana.

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    Te murunga roa: Ko nga turoro i tukinotia ki te FUCASO kua whakaatu i te 12-marama Progression-Free Survival (PFS) reiti o 85.5%, e tohu ana i te murunga mo te wa roa me te pai ake o te oranga.

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    Kōtaha Haumaru: Ki te ≥3 grade Cytokine Release Syndrome (CRS) ka puta i roto i te 1% anake o nga turoro me te kore korero mo te ≥3 grade Immune Effector Cell-Associated Neurotoxicity Syndrome (ICANS), ka tuku a FUCASO i tetahi waahanga maimoatanga haumaru ake ki etahi atu maimoatanga CAR-T.

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    Utu-Painga: He iti ake te utu mo te maimoatanga FUCASO i nga rongoa rite e waatea ana i te United States, na te mea he whiringa pai mo te whānuitanga o nga turoro.

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    Tae Ao: Kua whakaturia e IASO BIO he whatunga pokapū maimoatanga matawhānui i Haina, e kaha ana ki te mahi i nga turoro mai i te ao katoa me nga ratonga whakauru mai i te whakawhitiwhiti korero ki te tiaki i muri i te maimoatanga.

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    Angitu Haumanu

    Ko te manawanui tuatahi i rongoatia ki te FUCASO kua eke ki te rima tau o te oranga kore mate pukupuku, he tohu whakamiharo i whakaritea ki te tau waenga Progression-Free Survival (PFS) o te 2.9 marama noa me te tiaki paerewa. E whakaatu ana tenei i te kaha o FUCASO ki te huri i te whenua maimoatanga mo te mate myeloma maha.

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