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Sabuwar Maganin Halitta Yana Ba da Sabon Fata ga Marasa Lafiyar Sickle Cell da Thalassemia

Hemo-cel, yana wakiltar wani ci gaba mai ban mamaki a fannin maganin cutar sikila (SCD) ta hanyar fasahar gyaran kwayoyin halitta ta CRISPR/Cas9. Wannan sabuwar hanyar magani tana ba da sabon bege ta hanyar ƙara yawan matakan haemoglobin na tayi (HbF), wanda zai iya inganta sakamakon marasa lafiya sosai.

    cikakken bayani game da samfurin

    Sabuwar Maganin Halitta Yana Ba da Sabon Fata ga Marasa Lafiyar Sickle Cell da Thalassemia

    Gyaran Halitta da Maganin Thalassemia (12) Hoto[24].jpg Gyaran Halitta da Maganin Thalassemia 3Hoto[24].jpg

    A wani ci gaba mai ban mamaki ga marasa lafiya da ke fama da cutar sikila (SCD) da thalassemia, wani sabon maganin kwayoyin halitta yana nuna babban nasara. Wannan maganin, wanda ke amfani da fasahar gyaran kwayoyin halitta ta CRISPR/Cas9 mai ci gaba, ya nuna nasarar warkewa 100% a gwaje-gwajen asibiti, yana ba da sabon bege ga waɗanda ke fama da waɗannan matsalolin jini masu tsanani.

    Maganin, wanda aka haɓaka tare da dandamalin ModiHSC® na musamman, yana mai da hankali kan tushen kwayoyin halitta na SCD da thalassemia. Ta hanyar gyara ingantaccen mai haɓaka BCL11A a cikin ƙwayoyin halittar jini da na haihuwa, maganin yana ba jiki damar samar da matakan haemoglobin na tayi (HbF). An nuna cewa matakan HbF masu yawa suna magance illolin cutar sickle hemoglobin (HbS) da rage alamun SCD da thalassemia, gami da hana rikice-rikicen vaso-occlusive da rage yawan anemia na hemolytic.

    1].jpg         2.jpg

    BIOOCUS, wata babbar runduna a fannin maganin kwayoyin halitta, tare da hadin gwiwar Asibitin Lu Daopei, ta taka muhimmiyar rawa wajen kawo wannan sabuwar hanyar magani ga marasa lafiya. 

    Nasarar da aka samu a fannin maganin ba ta misaltuwa, inda aka yi wa marasa lafiya 15 magani zuwa yanzu, duk sun sami cikakkiyar gafara da kuma ci gaba mai kyau a cikin ingancin rayuwarsu. Wannan kashi 100% na maganin yana da matuƙar muhimmanci a yaƙi da cutar SCD da thalassemia.

     

    Maganin ya samu karbuwa a duniya baki daya, inda kwararru a fadin duniya suka yaba da shi a matsayin wani ci gaba a fannin magance matsalolin jinin kwayoyin halitta. Ya shahara ba kawai saboda ingancinsa ba har ma da ingancinsa na farashi. Ba kamar sauran magungunan kwayoyin halitta ba, wadanda za su iya zama masu tsada sosai, wannan maganin yana bayar da tsarin farashi mai sauki, wanda hakan ya sanya ya zama zabi mai kyau ga marasa lafiya da dama.

    A wani yanayi mai tsauri, wani majiyyaci ɗan shekara 12 da ke fama da rikice-rikicen jijiyoyin jini da kuma mummunan anemia na jini ya fuskanci ƙarshen alamun bayan an yi masa magani da wannan maganin kwayoyin halitta. Wannan lamarin, da sauransu, yana nuna yuwuwar sauyi a cikin maganin ga marasa lafiya da ke fama da SCD da thalassemia a duk duniya.

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    Yayin da BIOOCUS ke ci gaba da faɗaɗa samuwar wannan maganin, gami da gwaje-gwajen asibiti da ke tafe a China, makomar tana da kyau ga waɗanda ke fama da waɗannan cututtuka masu ƙalubale. Tare da goyon bayan Asibitin Lu Daopei, wannan maganin zai sake fasalta matsayin kulawa ga SCD da thalassemia, yana ba da sabuwar rayuwa ga marasa lafiya marasa adadi.

    Idan kai ko wani ƙaunatacce yana fama da cutar sikila ko thalassemia kuma kuna da sha'awar bincika wannan sabuwar hanyar magani, muna gayyatarku da ku tuntube mu. Ƙungiyarmu a shirye take don samar muku da tallafi da bayanai da kuke buƙata don yanke shawara mai kyau game da tafiyarku ta kiwon lafiya.

    Cirewar Hemo-cel ta CRISPR[2] conv 1.png

    Cikakken Tallafi ga Marasa Lafiya na Ƙasashen Duniya da ke Tafiya zuwa China don Maganin Hemo-cel

    A BIOOCUS, mun himmatu wajen samar da kulawa da tallafi na musamman ga marasa lafiya na ƙasashen waje da ke fama da cutar thalassemia ko sickle cell da ke neman maganin Hemo-cel a China. Ayyukanmu masu cikakken tsari sun ƙunshi kowane mataki na tafiya, tun daga shirye-shiryen kafin tafiya zuwa kulawar bayan magani.

    1. Shiri Kafin Tafiya

    Kafin tafiya, marasa lafiya za su yi cikakken bincike a asibitocin yankinsu. Wannan ya haɗa da cikakken kimanta tarihin lafiya, sa ido kan alamun cutar, gwaje-gwajen jini, da takamaiman gwaje-gwaje da aka tsara don cutar thalassemia ko sickle cell. Muna tabbatar da cewa an tattara duk takardun likita, gami da bayanan jini da tabbatar da ganewar asali, kuma an aika su zuwa cibiyarmu don dubawa.

    2. Tafiya da Asibiti

    Muna sauƙaƙa dukkan tsarin tafiya, gami da shirya wuraren ajiye marasa lafiya a asibitoci da aka keɓe. Ana jagorantar marasa lafiya ta hanyar tsarin shiga asibiti bayan isowa, wanda ke tabbatar da cewa an samu sauyi cikin sauƙi zuwa magani.

    3. Tsarin Magani

    Bayan an kwantar da marasa lafiya, za a yi musu gwaje-gwaje na farko. Idan aka ga sun cancanta, za a fara tattarawa da kuma tattara ƙwayoyin halittar jini. Ana aika waɗannan ƙwayoyin zuwa cibiyarmu ta GMP don kula da inganci da ƙera su, inda marasa lafiya za su iya komawa ƙasarsu don jiran ƙarin umarni.

    4. Dashen dashen da kuma Kula da Masu Kula da shi

    Da zarar an amince da ƙwayoyin halittar da aka shirya, marasa lafiya za su dawo don a dasa su. Ƙungiyarmu ta himmatu wajen samar da tallafi mai ɗorewa a duk tsawon lokacin da ake ɗauka a asibiti, tare da tabbatar da cewa kowane majiyyaci ya sami kulawa ta musamman. Bayan an sallame shi, muna daidaita gwaje-gwaje na ci gaba akai-akai don sa ido kan murmurewa da walwala.

    A BIOOCUS, muna ba da fifiko ga lafiya da jin daɗin marasa lafiyarmu na ƙasashen waje, muna yin duk mai yiwuwa don samar da ƙwarewar magani mai tallafi da cikakken bayani. Don ƙarin bayani game da ayyukanmu, da fatan za a tuntuɓe mu.

     

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